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STATEMENTS OF OPERATIONS (USD $)
12 Months Ended
Dec. 31, 2014
Dec. 31, 2013
Dec. 31, 2012
Revenue:      
Licensing revenue $ 100,000us-gaap_LicensesRevenue $ 300,000us-gaap_LicensesRevenue $ 100,000us-gaap_LicensesRevenue
Expenses:      
Research and development 36,677,706us-gaap_ResearchAndDevelopmentExpense 17,500,469us-gaap_ResearchAndDevelopmentExpense 12,684,793us-gaap_ResearchAndDevelopmentExpense
General and administrative 12,845,231us-gaap_GeneralAndAdministrativeExpense 10,273,576us-gaap_GeneralAndAdministrativeExpense 8,353,330us-gaap_GeneralAndAdministrativeExpense
Depreciation and amortization 182,927us-gaap_DepreciationAndAmortization 120,399us-gaap_DepreciationAndAmortization 113,936us-gaap_DepreciationAndAmortization
Total expenses 49,705,864us-gaap_CostsAndExpenses 27,894,444us-gaap_CostsAndExpenses 21,152,059us-gaap_CostsAndExpenses
Loss before other income (loss) (49,605,864)us-gaap_OperatingIncomeLoss (27,594,444)us-gaap_OperatingIncomeLoss (21,052,059)us-gaap_OperatingIncomeLoss
Other income (loss):      
Interest income 305,331us-gaap_InvestmentIncomeInterestAndDividend 137,676us-gaap_InvestmentIncomeInterestAndDividend 131,666us-gaap_InvestmentIncomeInterestAndDividend
Other income, net 132,114us-gaap_OtherNonoperatingIncome 183,025us-gaap_OtherNonoperatingIncome 191,416us-gaap_OtherNonoperatingIncome
(Gain) loss on warrant liability 19,051,239us-gaap_DerivativeGainLossOnDerivativeNet (20,210,094)us-gaap_DerivativeGainLossOnDerivativeNet 2,766,704us-gaap_DerivativeGainLossOnDerivativeNet
Loss before provision for income taxes (30,117,180)us-gaap_IncomeLossFromContinuingOperationsBeforeIncomeTaxesExtraordinaryItemsNoncontrollingInterest (47,483,837)us-gaap_IncomeLossFromContinuingOperationsBeforeIncomeTaxesExtraordinaryItemsNoncontrollingInterest (17,962,273)us-gaap_IncomeLossFromContinuingOperationsBeforeIncomeTaxesExtraordinaryItemsNoncontrollingInterest
Income tax expense (800)us-gaap_IncomeTaxExpenseBenefit (1,600)us-gaap_IncomeTaxExpenseBenefit (1,600)us-gaap_IncomeTaxExpenseBenefit
Net loss $ (30,117,980)us-gaap_NetIncomeLoss $ (47,485,437)us-gaap_NetIncomeLoss $ (17,963,873)us-gaap_NetIncomeLoss
Basic and diluted loss per share $ (0.55)us-gaap_EarningsPerShareBasicAndDiluted $ (1.44)us-gaap_EarningsPerShareBasicAndDiluted $ (0.78)us-gaap_EarningsPerShareBasicAndDiluted
Basic weighted average shares outstanding (in shares) 54,371,151us-gaap_WeightedAverageNumberOfSharesOutstandingBasic 32,891,202us-gaap_WeightedAverageNumberOfSharesOutstandingBasic 22,973,905us-gaap_WeightedAverageNumberOfSharesOutstandingBasic
Diluted weighted average shares outstanding (in shares) 54,371,151us-gaap_WeightedAverageNumberOfDilutedSharesOutstanding 32,891,202us-gaap_WeightedAverageNumberOfDilutedSharesOutstanding 22,973,905us-gaap_WeightedAverageNumberOfDilutedSharesOutstanding