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Research, Collaboration and License Agreements - Additional Information (Details)
1 Months Ended 3 Months Ended 6 Months Ended 12 Months Ended
Mar. 31, 2021
USD ($)
Oct. 31, 2020
USD ($)
Aug. 31, 2020
USD ($)
Apr. 30, 2020
Product
Dec. 31, 2019
USD ($)
Jun. 30, 2021
USD ($)
shares
Jun. 30, 2020
USD ($)
Mar. 31, 2020
USD ($)
shares
Jun. 30, 2021
USD ($)
shares
Jun. 30, 2020
USD ($)
Dec. 31, 2020
USD ($)
shares
Oct. 29, 2020
USD ($)
Feb. 21, 2020
USD ($)
Nov. 30, 2019
shares
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Common stock, shares issued | shares           38,391,165     38,391,165   37,761,435      
Research and development           $ 30,643,000 $ 3,062,000   $ 54,497,000 $ 8,576,000        
TSHA-120                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Additional milestone payments                 0          
Research and development $ 5,500,000                          
Upfront payment 5,500,000                          
Clinical, regulatory and commercial milestones to be received $ 19,300,000                          
UT Southwestern Agreement                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Preclinical activities period under sponsored research agreements       2 years                    
Minimum licensed product to develop obtain regulatory approval for and commercialize | Product       1                    
Common stock, shares issued | shares               0           2,179,000
Percentage of fully diluted common stock shares outstanding                           20.00%
Percentage of entitled to receive additional shares on fully diluted basis                           10.00%
Queen's Agreement                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Research grant of committed fund amount         $ 3,800,000                  
Percentage of interest rate         6.00%                  
Research grant outstanding fund amount                     $ 0      
Additional milestone payments                 0          
Queen's Agreement | Research and Development Expense                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Cash payment to acquire license agreement               $ 3,000,000.0            
Queen's Agreement | Maximum                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
License agreement regulatory milestones payment                         $ 10,000,000.0  
License agreement commercial milestones payment                         $ 10,000,000.0  
Abeona CLN1 Agreements                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Additional milestone payments                 0          
License fee payment     $ 3,000,000.0                      
Purchase of clinical materials and reimbursement incurred development costs   $ 4,000,000.0                        
Research and development                     7,000,000.0      
Abeona CLN1 Agreements | Maximum                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
License and inventory purchase agreement regulatory related milestones payment     26,000,000.0                      
License and inventory purchase agreement sales related milestones payment     $ 30,000,000.0                      
Abeona | Abeona Rett Agreement                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Additional milestone payments                 $ 0          
Payment of one-time upfront license fee                     $ 3,000,000.0      
Abeona | Maximum | Abeona Rett Agreement                            
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]                            
Regulatory related milestones obligation payable                       $ 26,500,000    
Sale-related milestones per licensed product and royalties on net sales of licensed products payable                       $ 30,000,000.0