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Consolidated Balance Sheets - USD ($)
Sep. 30, 2016
Dec. 31, 2015
Current assets:    
Cash and cash equivalents $ 320,078,000 $ 186,753,000
Marketable securities 111,192,000 0
Prepaid expenses and other current assets 3,418,000 1,738,000
Total current assets 434,688,000 188,491,000
Property and equipment, net 1,049,000 286,000
Restricted cash 564,000 39,000
Deferred offering costs   200,000
Total assets 436,301,000 189,016,000
Current liabilities:    
Accounts payable 5,237,000 5,159,000
Accrued expenses 17,093,000 10,148,000
Total current liabilities 22,330,000 15,307,000
Other liabilities 234,000 14,000
Total liabilities 22,564,000 15,321,000
Commitments and contingencies (Note 5)
Stockholders’ equity:    
Preferred stock, $0.0001 par value per share; 5,000,000 shares authorized at September 30, 2016 and December 31, 2015, respectively; no shares issued or outstanding at September 30, 2016 and December 31, 2015, respectively
Common stock, $0.0001 par value per share; 120,000,000 shares authorized at September 30, 2016 and December 31, 2015, respectively; 37,165,124 and 28,823,549 shares issued and outstanding at September 30, 2016 and December 31, 2015, respectively 4,000 3,000
Additional paid-in capital 678,194,000 335,032,000
Accumulated deficit (264,426,000) (161,340,000)
Accumulated other comprehensive items (35,000)  
Total stockholders’ equity 413,737,000 173,695,000
Total liabilities and stockholders’ equity $ 436,301,000 $ 189,016,000