XML 14 R2.htm IDEA: XBRL DOCUMENT v3.26.1
Condensed Consolidated Balance Sheets (Unaudited) - USD ($)
$ in Thousands
3 Months Ended
Mar. 31, 2026
Dec. 31, 2025
Current assets:    
Cash and cash equivalents $ 23,706 $ 18,008
Investments in marketable short-term securities 71,520 73,463
Accounts receivable 1,312 1,447
License receivable from Genevant 178,741 0
Prepaid expenses and other current assets 1,732 1,538
Total current assets 277,011 94,456
Property and equipment, net of accumulated depreciation and impairment of $224 (December 31, 2025: $213) 22 32
Other non-current assets 131 130
Total assets 277,164 94,618
Current liabilities:    
Accounts payable and accrued liabilities 4,474 5,459
Lease liability, current 631 547
Total current liabilities 5,105 6,006
Liability related to sale of future royalties 3,278 3,442
Contingent consideration 8,604 8,395
Lease liability, non-current 0 199
Total liabilities 16,987 18,042
Stockholders’ equity    
Issued and outstanding: 196,947,757 (December 31, 2025: 192,531,225) 1,444,494 1,421,429
Additional paid-in capital 74,256 83,318
Deficit (1,210,378) (1,380,073)
Accumulated other comprehensive loss (48,195) (48,098)
Total stockholders’ equity 260,177 76,576
Total liabilities and stockholders’ equity $ 277,164 $ 94,618
Common Stock, Shares Authorized, Unlimited [Fixed List] Unlimited