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Balance Sheets - USD ($)
$ in Thousands
Dec. 31, 2014
Dec. 31, 2013
Current assets    
Cash and cash equivalents $ 39,814 $ 210,596
Due from Novartis Pharma, AG 960  
Available for sale securities 423,746  
Prepaid expenses and other current assets 8,812 6,804
Deferred tax assets 50  
Total current assets 473,382 217,400
Property and equipment, net 1,555 27
Deferred tax assets, non-current 4,467  
Security deposits 282 255
Other assets 100  
Total assets 479,786 217,682
Current liabilities    
Accounts payable and accrued expenses 8,707 3,810
Accrued research and development expenses 7,918 2,485
Deferred revenue 3,206  
Total current liabilities 19,831 6,295
Deferred revenue, long-term 206,418  
Royalty purchase liability 125,000 41,667
Total liabilities 351,249 47,962
Stockholders' equity    
Common stock - $0.001 par value, 200,000,000 shares authorized, 33,994,520 and 31,413,208 shares issued and outstanding at December 31, 2014 and December 31, 2013, respectively 34 31
Additional paid-in capital 428,390 352,739
Accumulated deficit (299,822) (183,050)
Accumulated other comprehensive loss (65)  
Total stockholders' equity 128,537 169,720
Total liabilities and stockholders' equity $ 479,786 $ 217,682
Preferred stock    
Stockholders' equity    
Preferred stock - $0.001 par value, 5,000,000 shares authorized, no shares issued or outstanding