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Balance Sheets (USD $)
In Thousands, unless otherwise specified
Sep. 30, 2013
Dec. 31, 2012
Current assets    
Cash and cash equivalents $ 236,079 $ 4,304
Prepaid expenses and other current assets 2,096 44
Other Assets   331
Security deposits 158 158
Total current assets 238,333 4,837
Property, plant and equipment, net 32 42
Other long term assets 11  
Total assets 238,376 4,879
Current liabilities    
Accrued clinical drug supplies and trial costs 3,477 1,013
Accounts payable and accrued expenses 4,431 1,391
Notes payable   11,040
Warrant liability   966
Total current liabilities 7,908 14,410
Royalty purchase liability 41,667  
Total liabilities 49,575 14,410
Stockholders' equity (deficit)    
Common stock - $0.001 par value, 200,000,000 shares authorized, 31,250,817 shares issued and outstanding at September 30, 2013; 155,864,851 shares authorized, 1,469,798 shares issued and outstanding at December 31, 2012 31 1
Additional paid-in capital 351,431  
Deficit accumulated during development stage (162,661) (126,471)
Total stockholders' equity (deficit) 188,801 (123,470)
Total liabilities and stockholders' equity (deficit) 238,376 4,879
Convertible and redeemable preferred stock
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   113,939
Series A
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   69,471
Series A-1
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   8,460
Series B
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   35,456
Series B-1
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   552
Junior Series A Convertible Preferred Stock
   
Stockholders' equity (deficit)    
Preferred Stock   3,000
Preferred stock
   
Stockholders' equity (deficit)    
Preferred Stock