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Balance Sheets (USD $)
In Thousands, unless otherwise specified
Dec. 31, 2013
Dec. 31, 2012
Current assets    
Cash and cash equivalents $ 210,596 $ 4,304
Prepaid expenses and other current assets 6,804 44
Other Assets   331
Security deposits   158
Total current assets 217,400 4,837
Property, plant and equipment, net 27 42
Security deposits 255  
Total assets 217,682 4,879
Current liabilities    
Accrued clinical drug supplies and trial costs 2,485 1,013
Accounts payable and accrued expenses 3,810 1,391
Notes payable   11,040
Warrant liability   966
Total current liabilities 6,295 14,410
Royalty purchase liability 41,667  
Total liabilities 47,962 14,410
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   113,939
Stockholders' equity (deficit)    
Common stock - $0.001 par value, 200,000,000 shares authorized, 31,413,208 shares issued and outstanding at December 31, 2013; 155,864,851 shares authorized, 1,469,798 shares issued and outstanding at December 31, 2012 31 1
Additional paid-in capital 352,739  
Deficit accumulated during development stage (183,050) (126,471)
Total stockholders' equity (deficit) 169,720 (123,470)
Total liabilities and stockholders' equity (deficit) 217,682 4,879
Series A
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   69,471
Series A-1
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   8,460
Series B
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   35,456
Series B-1
   
Preferred Stock, Convertible and Redeemable:    
Total Preferred Stock, Convertible and Redeemable   552
Junior Series A Convertible Preferred Stock
   
Stockholders' equity (deficit)    
Preferred Stock   3,000
Preferred stock
   
Stockholders' equity (deficit)    
Preferred Stock