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CONDENSED BALANCE SHEETS - USD ($)
Mar. 31, 2018
Dec. 31, 2017
Current assets:    
Cash and cash equivalents at carrying value $ 89,831,744 $ 18,559,130
Short-term investments 83,292,883 78,912,297
Receivables   273,044
Prepaid expenses 1,259,420 751,255
Other assets 172,390 77,077
Total current assets 174,556,437 98,572,803
Property and equipment, net 1,942,852 2,182,399
Other noncurrent assets 178,941 7,067
Total assets 176,678,230 100,762,269
Current liabilities:    
Accounts payable 1,414,607 376,394
Accrued wages and benefits 1,120,772 2,533,133
Accrued clinical trial expenses 1,007,396 689,985
Accrued expenses and other liabilities 1,070,302 946,668
Total current liabilities 4,613,077 4,546,180
Deferred revenue, net of current portion 363,266 731,944
Total liabilities 4,976,343 5,278,124
Stockholders’ equity:    
Common stock: $0.001 par value, 100,000,000 shares authorized; 48,203,529 and 69,427,773 shares issued and outstanding at December 31, 2017 and March 31, 2018 69,428 48,204
Additional paid-in capital 488,929,377 404,454,909
Accumulated other comprehensive (loss) income (79,143) (64,433)
Retained deficit (317,217,775) (308,954,535)
Total stockholders’ equity 171,701,887 95,484,145
Total liabilities and stockholders’ equity $ 176,678,230 $ 100,762,269