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CONDENSED BALANCE SHEETS - USD ($)
Sep. 30, 2017
Dec. 31, 2016
Current assets:    
Cash and cash equivalents at carrying value $ 47,178,505 $ 31,228,192
Short-term investments 55,901,729 106,979,224
Receivables 27,746 55,074
Prepaid expenses 1,159,139 1,737,308
Other assets 125,435 255,912
Total current assets 104,392,554 140,255,710
Property and equipment, net 2,445,550 3,205,077
Other noncurrent assets 7,067 33,567
Total assets 106,845,171 143,494,354
Current liabilities:    
Accounts payable 395,046 1,381,545
Accrued wages and benefits 1,542,864 2,705,475
Accrued clinical trial expenses 1,360,587 861,293
Accrued expenses and other liabilities 1,048,764 613,861
Total current liabilities 4,347,261 5,562,174
Other liabilities, net of current portion   2,873
Deferred revenue, net of current portion 744,444 781,944
Total liabilities 5,091,705 6,346,991
Stockholders’ equity:    
Common stock: $0.001 par value, 100,000,000 shares authorized; 42,377,522 and 42,859,381 shares issued and outstanding at December 31, 2016 and September 30, 2017 47,860 42,378
Additional paid-in capital 402,100,682 390,768,742
Accumulated other comprehensive (loss) income (4,560) (41,196)
Retained deficit (300,390,516) (253,622,561)
Total stockholders’ equity 101,753,466 137,147,363
Total liabilities and stockholders’ equity $ 106,845,171 $ 143,494,354