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MAJOR CUSTOMERS, PARTNERSHIPS AND STRATEGIC ALLIANCES - Pfizer Inc. (Narrative) (Details)
1 Months Ended 12 Months Ended 37 Months Ended 44 Months Ended 97 Months Ended 104 Months Ended
Oct. 27, 2025
USD ($)
Dec. 31, 2024
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Dec. 31, 2017
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May 31, 2017
USD ($)
Dec. 31, 2025
USD ($)
Dec. 31, 2024
USD ($)
Dec. 31, 2020
USD ($)
Dec. 31, 2020
USD ($)
Dec. 31, 2025
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Dec. 31, 2025
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milestone
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Revenues         $ 39,552,000 $ 57,800,000        
Revenue, performance obligation, termination Fee, consideration receivable   $ 5,000,000.0       5,000,000.0        
Pfizer                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Agreement termination, term (in years)       15 years            
Pfizer | License                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Revenues under agreement       $ 70,000,000.0            
Potential amount to be funded for achievement of specified commercialized and sales milestones       $ 266,500,000            
Collaborative arrangement, number of milestones achieved | milestone                   2
Milestone payments received                   $ 55,000,000.0
Revenues $ 6,000,000.0         $ 0   $ 134,000,000.0    
Revenue, performance obligation, termination fee, payable term (in days)           60 days        
Revenue, performance obligation, termination fee, payable term if sublicense transfers (in days)   30 days                
Pfizer | License | Certain Zinc Finger Nucleases (ZFN) Agreement                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Revenues         6,000,000.0          
Pfizer | License | AAV Delivery System                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Revenues         5,000,000.0          
Pfizer | License | Minimum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty (as a percent)       14.00%            
Pfizer | License | Maximum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty (as a percent)       20.00%            
Pfizer | License | Achievement of specified clinical development intellectual property and regulatory milestones                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Development and sales-based milestone payments to be received       $ 208,500,000            
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Agreement termination, term (in years)     15 years              
Milestone payments received     $ 12,000,000.0              
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Milestone payments received                 $ 5,000,000.0  
Revenues         $ 0 $ 0 $ 17,000,000.0      
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License | Minimum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty (as a percent)     14.00%              
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License | Maximum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty (as a percent)     20.00%